STAT

Roivant immune drug significantly outperformed placebo in treating rare skin disease

In a small trial, Roivant's immune drug significantly outperformed placebo in clearing lesions caused by a rare skin disease.
News-Medical.Net

First topical CRISPR gene therapy corrects disease-causing mutations in human skin

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

A skin biopsy can detect a rare neurodegenerative disease

By determining the structure of the deposits responsible for transthyretin amyloidosis through a simple skin biopsy, scientists at UNIGE are paving the way for a new diagnostic method for ...
Yahoo

‘Like being burned from the inside out’: Utah woman describes rare skin disease caused by medication

SALT LAKE CITY (ABC4) — A Utah woman is sharing her story after she survived an incredibly rare and often fatal skin disorder caused by an allergic reaction to antibiotics. Brandi Nicole Pond, who ...
Forbes

Breakthrough Gene Therapy For Butterfly Children’s Disease

A revolutionary treatment brings new hope to those suffering from a devastating rare skin disorder, while showcasing an innovative funding model that could transform rare disease research In a ...
Arizona Daily Sun

FDA approves first cell-based gene therapy for rare genetic skin disorder

U.S. Food and Drug Administration on Tuesday approved Abeona Therapeutics' gene therapy for a rare skin disorder. The gene therapy, called Zevaskyn, is approved to treat adult and pediatric patients ...
Hosted on MSN

‘Like being burned from the inside out’: Woman describes rare skin disease caused by medication

SALT LAKE CITY (KTVX) — A Utah woman is sharing her story after she survived an incredibly rare and often fatal skin disorder caused by an allergic reaction to antibiotics. “I’m lucky to be alive, I’m ...
University of Geneva

A skin biopsy to detect a rare neurodegenerative disease

By determining the structure of the deposits responsible for transthyretin amyloidosis through a simple skin biopsy, scientists at UNIGE are paving the way for a new diagnostic method for ...
WGNO

‘Like being burned from the inside out’: Utah woman describes rare skin disease caused by medication

SALT LAKE CITY (KTVX) — A Utah woman is sharing her story after she survived an incredibly rare and often fatal skin disorder caused by an allergic reaction to antibiotics. “I’m lucky to be alive, I’m ...