A team of researchers at the Broad Institute, led by gene-editing pioneer David Liu, has developed a new genome-editing ...

PERT edits the genome to permanently express a suppressor tRNA, so that cells affected by nonsense mutations can produce functional protein.

JScreen, an organization that encourages people to undergo testing for genetic diseases, has launched a campaign highlighting families who lost children to Tay-Sachs disease. Tay-Sachs is a rare ...

Rodolphe Barrangou, a genomic-editing expert at North Carolina State University who was not involved in the research, said ...

PASCO COUNTY, Fla. (WFLA) — For parents with children with Tay Sachs disease, there’s often little hope, no treatment, and no cure. It’s a rare and deadly disease that attacks the nerve cells in the ...

Tay Sachs is a devastating genetic disease with no known cure. But now, experts are hoping a new push for awareness could help parents down the road.

Jews who are considering starting a family or who are just worried about their own health are being encouraged to get tested, as Feb. 5 through Feb. 11 marks Jewish Genetic Screening Awareness Week.

Dr. Matt Goldstein and Myra Sack lost their daughter, Havi, to Tay-Sachs disease in 2021. Tay-Sachs is a rare, inherited genetic disease primarily affecting infants and young children. There is no ...

Scientists from MIT and Harvard present a new strategy called PERT in 'Nature'. Instead of correcting gene by gene, they use ...

(RNS) — Some 25 years ago, a friend of mine and his wife whose little boy had been diagnosed with Tay-Sachs disease visited our home. A relatively rare genetic disorder that is less so among ...

Stewart Altman, wheelchair-bound, fights for cure as gene therapy shows promise. May 13, 2011— -- For 26 years, doctors could not piece together the medical puzzle of Stewart Altman's symptoms -- ...