Asperger’s syndrome is part of the autism spectrum. It shares many features with other types of autism, such as a need for routine. It is also marked by strong intellectual and verbal ...

Ultragenyx Pharmaceuticals' GTX-102 earns FDA Breakthrough status after early data shows sustained progress in Angelman syndrome patients.

NOVATO, Calif., June 27, 2025 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), today announced that it has ...