PTC axes utreloxastat program after phase 2 ALS failure
But utreloxastat had little effect on ALS in the phase 2 trial. PTC powered the study to show whether twice-daily oral dosing of utreloxastat could achieve a two-point difference on ALSFRS, an instrument for evaluating the functional status of ALS patients. The drug candidate fell short of that bar.
ALS is a progressive neurodegenerative disease — and there is no cure. Brunner, who was running 3 miles a day at the onset of ...
23hon MSN
Since Jimmer Szatkowski opened Upstate New York’s first Chick-fil-A in 2018, he’s been at the restaurant most every day. He’s ...
Despite the “unfortunate” failure, William Blair analysts do not believe that the utreloxastat readout will heavily affect ...
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'Exercise juice' released by muscles helps nerves grow, study findsIn a new study of mouse cells, scientists found that both the biochemical and mechanical effects of exercise may help injured ...
18hon MSN
Thompson, who has spent the latter part of his coaching career while suffering from ALS, is much more than a fine football ...
PTC Therapeutics may reeling from the failure of its amyotrophic lateral sclerosis (ALS) drug utreloxastat yesterday, but the ...
MaaT Pharma Announces Positive Phase 1b Results, Meeting Primary Endpoint in the Evaluation of MaaT033 in Amyotrophic Lateral ...
There are now at least two patients who have had Neuralink's brain chip implanted in their head. While there have been some ...
A team from IIT-BHU is developing a revolutionary cell-based device using 3D bioprinting technology to potentially cure ...
Sydney, Australia, 28 November 2024 – Celosia Therapeutics, an Australian biotech company developing advanced gene therapies for neurodegenerative diseases, has completed one of the largest Series A ...
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