NOVATO, Calif., June 27, 2025 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), today announced that it has ...

Colin Farrell opened up to PEOPLE about his son James, who was diagnosed with Angelman syndrome. Here’s what to know about the rare neurogenetic disorder that affects 1 in 15,000 people.

Ultragenyx Pharmaceuticals' GTX-102 earns FDA Breakthrough status after early data shows sustained progress in Angelman syndrome patients.

Both TEGSEDI and WAYLIVRA are legacy assets that were originally brought to the EU market via an Ionis subsidiary, Akcea ...

Other companies working on antisense treatments for Angelman syndrome include Ultragenyx, which reported positive phase 1/2 results with its GTX-102 drug earlier this year, and Roche/Genentech ...

Financial giant UBS has declared that enough is enough with lagging healthcare valuations – and now believes it will be the ...

BACKGROUND Angelman syndrome (AS) is a severe neurobehavioural disorder caused by defects in the maternally derived imprinted domain located on 15q11-q13. Most patients acquire AS by one of five ...

Use precise geolocation data. Actively scan device characteristics for identification. Store and/or access information on a ...

Use precise geolocation data. Actively scan device characteristics for identification. Store and/or access information on a ...

This first phase marks a major milestone in the transformation of Canary Wharf into one of the most digitally advanced commercial districts in the world. Completed installations include a suite of ...